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The global impact of Precision Medicine Group.
As it happens.

Impact, observations, and insights on the evolving healthcare landscape.

On Demand: Cell and Gene Therapies – How High Can Prices Go?

2023-07-18T16:07:02-04:00Cell & Gene Therapy, Events, Thought Leadership|

Join our experts on April 26, 2023 at 9AM EST as we dive into a powerful 30 minute webinar followed by live Q&A.

This ON24 webinar will discuss how cell and gene therapies can be justifiably priced at different levels. We will explore just how high they can extend and also how we can collectively ensure that patients can access these innovations when they are needed. This discussion will be led by David Carr: Senior Director, Global Pricing and Market Access (PRECISIONadvisors), Richard Macaulay: SVP, Global Pricing and Market Access (PRECISIONadvisors).

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White Paper: “Preventative” Gene Therapies: Perspectives on Payer Access Challenges and Solutions

2023-11-09T08:32:51-05:00Cell & Gene Therapy, News, Thought Leadership|

Gene therapies offer hope for patients with severe genetic diseases by providing long-term benefits and even cures. However, the challenges of evaluating the long-term benefits of these therapies from a payer perspective are considerable. This white paper by PRECISIONadvisors highlights the shift of gene therapy research into more prevalent diseases, and outlines how manufacturers and payers can co—create evidence requirements and models to optimize launch success and sustainability.

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Article: The Future of Gene Therapies: Three Trends

2023-06-06T14:38:00-04:00Cell & Gene Therapy|

Since the first gene therapy procedure more than 30 years ago, the field has seen significant advances and development, but also setbacks and issues. What is the future direction for gene therapies? Precision’s Phil Cyr, Richard Macaulay and Andy Kinley identify three future trends and how they might impact safety, manufacturing development, and reimbursement and payment.

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Conference: Meeting on the Med, 2023

2023-04-05T02:55:47-04:00Cell & Gene Therapy, Events, Thought Leadership|

Precision will be at this year’s Meeting on the Med, April 12-14, 2023, in Barcelona, Spain. Connect with our team of experts as they lead meaningful presentations and discussions throughout this event providing insights into the clinical development, manufacturing, and commercialization for cell and gene therapies.

Connect with our Advanced Therapy experts

  • Visit us through any of the numerous networking opportunities at Meeting on the Med 23′
  • Be sure to attend the ADVANCE sponsored workshop on April 12, 2023, at 4:45PM – 5:30PM CET |Location: Hotel Arts Barcelona (BioCentriq Ballroom: Gaudi 3)

You can register for Meeting on the Med below:

REGISTER HERE

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Article: The FDA and AAV-Based Gene Therapy Safety: What You Should Know

2023-07-11T09:35:59-04:00Cell & Gene Therapy|

Over the last couple of years, we have witnessed the tremendous potential of adeno-associated virus (AAV)-based gene therapies. However, there have been a few high-profile safety issues that have occurred, including deaths associated with AAV vector gene therapies that have raised safety concerns among the public and regulators. Don’t miss this great primer on AAV-based gene therapies by Precision’s Deb Phippard and Phil Cyr, including basic background on the vectors, safety concerns, strategies to mitigate safety issues, and recent FDA safety meetings.

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Conference: Gene Therapy for Rare Disorders (GTRD), 2023

2023-03-14T10:37:26-04:00Cell & Gene Therapy, Events, Thought Leadership|

Precision will be at this year’s Gene Therapy for Rare Disorders on March 20-23, 2023, in Boston, MA. Connect with our team of experts as they lead meaningful presentations and discussions throughout this event providing insights into the clinical development, manufacturing, and commercialization for gene therapies.

Speaking Engagements
Detailed descriptions for each speaking engagement are included below. 

  • Precision ADVANCE will have a plenary speaking position on March 21, 2023, 8:30 – 9:00 am.
  • Project Farma will be facilitating a plenary panel discussion ” Current Trends in Technical Operations for Rare Disorders” on March 21, 2023, 10:45 – 11:15 am.
  • Project Farma’s Tony Khoury (EVP, Project Farma) will be joining the Manufacturing track panel discussion, “Capacity versus Capability – Moving Towards Innovative Manufacturing Processes,” on March 21, 2023, 11:15 – 11:45 am.
  • Precision ADVANCE will hold a drinks reception on March 21, 2023, at 6:10 pm in the Grand & Liberty Ballroom.

Connect with our Advanced Therapy experts

  • Visit us at booth 13 in the exhibition area
  • Schedule in-person or virtual meetings by clicking here: https://bit.ly/precisionmedicinegrp
  • Attend our ADVANCE-sponsored Drinks Reception on March 21, 2023, at 6:10 PM ET

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Plenary Speaking Position: Successfully Launching a Gene Therapy with Cynthia Pussinen & Dave Lennon
Precision ADVANCE | March 21, 2023, 8:30 – 9AM ET 

  • Key Takeaways
    • Identify active strategies to enable a smooth plan from preclinical development to commercialization
    • New approaches for regulatory approval and commercialization
    • Anticipating and overcoming potential hurdles specific to gene therapies
    • The future of the industry

Speakers:

  • Anshul Mangal: President (Project Farma & Precision ADVANCE)
  • Cynthia Pussinen: Former CTO (Spark Therapeutics Inc.)
  • Dave Lennon: CEO (Satellite Bio)

Panel Discussion: Current Trends in Technical Operations for Rare Disorders
Project Farma | March 21, 2023, 10:45-11:15AM ET

  • Key Takeaways
    • Current trends impacting manufacturing of gene therapies including capital markets, supply chain and technologies
    • Shifts in technical operations as a result of current trends
    • Opportunities and innovations in technical operations that can transform the industry

Speakers:

  • [Moderator] Charlie Harper: Vice President, Consulting (Project Farma)
  • Greg Gara: Senior Vice President (Project Farma)
  • Tony Khoury: Executive Vice President (Project Farma)
  • Eric Hacherl: Vice President, Manufacturing (Spark Therapeutics, Inc.)

Panel Discussion: Manufacturing Track: Capacity versus Capability – Moving Towards Innovative Manufacturing Processes
Project Farma | March 21, 2023, 11:15 – 11:45AM ET

  • Greg Gara: Senior Vice President (Project Farma) to join
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Article: Weathering the Storm: Cell and Gene’s Economic Downturn

2023-02-21T15:29:48-05:00Cell & Gene Therapy|

After record-setting milestones in fundraising over the past two years, the advanced therapy investment landscape is experiencing a natural correction. Precision’s Anshul Mangal and Dr. James M. Wilson outline in this The Medicine Maker article how industry leaders can ensure the advancement of innovative treatments for patients with #rarediseases by consolidating investments and prioritizing partnerships with patient advocacy organizations.

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On-Demand: Let’s Talk: Moving CGTx Clinical Development Forward in 2023

2023-03-09T12:12:46-05:00Cell & Gene Therapy, Events|

Sponsored by Precision ADVANCE, this Endpoints webinar will convene leading advanced therapy experts to discuss the future of CGTx clinical development. This discussion will be moderated by Teresa Pokladowski: Regional VP, Clinical Business Solutions (Precision for Medicine), and include insights from Kinnari Patel: President & COO (Rocket Pharmaceuticals), Suma Krishnan: Founder & President (Kystal Biotech), Dawn Buchanan: VP Clinical Operations (AffyImmune), and Ramona Repaczki-Jones: Executive Director, Commercial Treatment Center Operations, Cell Therapy (lovance Biotherapeutics, Inc).

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White Paper: What’s Next for Cell and Gene Therapies in 2023 and Beyond

2023-02-09T13:57:47-05:00Cell & Gene Therapy, Thought Leadership|

The cell and gene therapy (CGTx) sector has flourished in recent years due to continued investor confidence. However, the present downturn in public markets has negatively affected that confidence, raising questions about the sector’s prospects for 2023 and beyond.

This white paper is based on a panel discussion at the Cell & Gene Meeting on the Mesa (October 11, 2022), sponsored by Precision ADVANCE, focusing on the future of advanced therapies. The panel included insights from the following industry leaders:

  • Anshul Mangal: President (Project Farma & Precision ADVANCE)
  • Stewart Abbot: Chief Scientific Officer (Turnstone Biologics)
  • Laura Lande-Diner: Chief Business Officer (Satellite Bio)
  • Robert Peters: Chief Scientific Officer (Ensoma)
  • Deborah Phippard: Chief Scientific Officer (Precision For Medicine)

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Precision Medicine Group is an integrated team of experts in fields from advanced lab sciences to translational informatics and regulatory affairs, payer insights to marketing communications. Together, we help our pharmaceutical and life-sciences clients conquer product development and commercialization challenges in a rapidly evolving environment.

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